At Neurogene we believe that innovation, robust scientific execution, and a strong sense of purpose are required to turn this promise into reality. Our focus is to develop life-changing …

Neurogene is focused on developing life-changing genetic medicines for patients and their families affected by rare, devastating neurological diseases. To accomplish this, we …

At Neurogene, our focus is to develop life-changing genetic medicines for patients and their families affected by rare, devastating neurological diseases.

Neurogene is a company founded on the vision to push the boundaries of genetic medicine to address complex and devastating neurological diseases, turning them into treatable conditions …

Today we are sharing an update regarding Neurogene’s ongoing Phase 1/2 open-label clinical trial evaluating the investigational gene therapy, NGN-401, in pediatric female participants …

Feb 24, 2025 · Neurogene has constructed a state-of-the-art gene therapy manufacturing facility in Houston, Texas. CGMP production of NGN-401 was conducted in this facility and will …

Neurogene is a company founded on the vision to push the boundaries of genetic medicine to address complex and devastating neurological diseases, turning them into treatable conditions …

Jul 18, 2023 · Proposed merger to create Nasdaq-listed biotech company focused on advancing Neurogene’s differentiated portfolio of genetic medicines for complex neurological diseases

At Neurogene, we focus on bringing life-changing genetic medicines to patients and families affected by rare, devastating neurological diseases. Our clinical-stage company is developing …

Neurogene’s lead Batten disease program is a gene therapy for the treatment of CLN5 Batten disease, a rapidly progressive neurodegenerative disease which primarily manifests during …