treatment Zolgensma died as a result of acute liver failure. The two fatalities were seen in children with the genetic neuromuscular wasting disease, according the pharma group, which said that ...

Liver toxicity is a known side effect that appears as a boxed warning on Zolgensma’s U.S. label ... the way across the spectrum of one specific disease,” he said. “That’s kind of a ...

Pause in UK access Meanwhile, access to Zolgensma in the UK has been suspended in children older than 12 completed months, as there have been a "small number" of cases of liver-related side ...

There were no reported cases of acute liver failure or bilirubin elevations ... In fiscal year 2023, Novartis reported Zolgensma sales of $1.21 billion. Zolgensma (onasemnogene abeparvovec ...