That’s because Kalydeco and its follow up Orkambi have only been of use to a subset of CF patients. But now the company is gaining real momentum, and its new drugs look set to bring it to a new ...

The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle ...

Vertex CEO Jeffrey Leiden has offered an olive branch to negotiators in the UK that could see the cystic fibrosis drug Orkambi finally supplied to patients in England. Leiden said that he is to ...