MedPage Today on MSN11h
Young Patient Dies After Receiving New Gene Therapy for Duchenne Muscular Dystrophy
A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
GEN - Genetic Engineering and Biotechnology News8h
DMD Patient Dies After Treatment with Sarepta Gene Therapy
The patient, whom Sarepta described as a young man and later told news outlets was 16 years old, suffered acute liver failure ...
Clinical Trials Arena on MSN16h
Avidity’s del-zota elicits 25% increase in dystrophin in DMD patients
The company plans to submit a biologics licence application to the US Food and Drug Administration later this year.
Fierce Pharma18h
Sarepta reports 1 death after patient received DMD gene therapy Elevidys
One patient with Duchenne muscular dystrophy (DMD) has passed away following treatment with Sarepta Therapeutics’ gene therapy Elevidys, the biotech ...
Clinical Trials Arena on MSN1d
Dyne’s DMD trial advances patient mobility and dystrophin expression
The Phase I/II Deliver trial sought to establish the impact of DYNE-251 on several mobility-related endpoints, seeing an ...
The American Journal of Managed Care19h
MRI Could Aid in Early Differential Diagnosis of DMD, BMD
Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular dystrophy early and improve the management of these conditions.