FDA Approves First Gene Therapy for Treatment of Aromatic L-amino Acid Decarboxylase Deficiency
The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus vector-based gene therapy indicated for the treatment of adult and pediatric patients ...
Microbial-based plastic shows potential for replacing PET bottles
Currently, the world is suffering from environmental problems caused by plastic waste. A KAIST research team has succeeded in ...
US FDA approves PTC Therapeutics' gene therapy for ultra-rare disorder
The U.S. Food and Drug Administration approved PTC Therapeutics' gene therapy to treat a potential fatal enzyme deficiency ...
Medpage Today on MSN3d
First Brain-Delivered Gene Therapy Approved for AADC Deficiency
The treatment is the first approved gene therapy for AADC deficiency, the FDA said. People with this rare disorder have ...
Nature7d
Transamination of Aromatic Ammo-Acids in Nervous Tissue
In this communication evidence is presented of transamination of aromatic amino-acids in the nervous tissues, that is, rat brain extracts.
EurekAlert!6d
A KAIST research team successfully produces microbial plastic to replace pet bottles
A team led by Distinguished Professor Sang Yup Lee of the Department of Chemical and Biomolecular Engineering has succeeded ...
FDA Approves PTC's Kebilidi As First Gene Therapy To Treat AADC Deficiency
The U.S. Food and Drug Administration approved PTC Therapeutics, Inc.'s Kebilidi (eladocagene exuparvovec-tneq) gene therapy for the ...
The American Journal of Managed Care2d
FDA Approves Gene Therapy to Treat AADC Deficiency
The approval marks the first time gene therapy will be available to treat patients with aromatic I-amino acid decarboxylase ...
emjreviews.com2d
FDA approves first gene therapy delivered directly to the brain
The drug is a treatment for a rare and fatal genetic disorder called aromatic l-amino acid decarboxylase (AADC) deficiency, ...
Engineering360 News6y
8: Aromatic Carboxylic Acids and Amides
An invaluable text for synthetic chemists in the pharmaceutical, agrochemical, plastic and detergent industries, this book provides a detailed, up-to-date account of the reactions of chlorosulfonic ...
Science Daily5d
Research team successfully produces microbial plastic to replace PET bottles
Researchers have succeeded in developing a microbial strain that efficiently produces pseudoaromatic polyester monomer to replace polyethylene terephthalate (PET) using systems metabolic engineering.